A methylation marker on the tRNA, and a new lipid nanoparticle, helps the ribosome ignore disease-causing mutations ...

Supportive therapy, like medications to help open the airways and heal infections, can help you live a healthier life and meet many of the challenges of this inherited respiratory condition. Share on ...

Breathing disorders are common in the U.S. with conditions like COPD affecting some 7% of the population and asthma affecting another 10%. Digestive conditions like GERD, acid reflux, Celiac disease ...

Atypical cystic fibrosis is a mild form of cystic fibrosis. People with this type of cystic fibrosis can experience symptoms that come and go or that are less severe than those people with classic ...

People with cystic fibrosis do not usually have a higher risk of COVID-19 when compared to people without this condition. They also typically have an infection course similar to people without cystic ...

For decades, lung disease has been the most visible and life-threatening part of cystic fibrosis. People might picture chronic (long-term) cough, breathlessness, recurrent chest infections and oxygen ...

A preclinical study combining chemically modified suppressor tRNAs with inhaled lipid nanoparticles has restored functional ...

Alyftrek (vanzacaftor/tezacaftor/deutivacaftor) is a combination medicine approved by the FDA in 2024. Alyftrek is approved to treat people ages 6 and older who have ...

Lung transplants are considered for individuals with end-stage cystic fibrosis when other treatments have failed to improve lung function and quality of life. However, lung transplants cannot cure ...

New combinations of molecules put many patients on the path to good health. But those with rarer mutations are, for now, left behind. Over the course of two decades spent developing treatments for the ...